An Evaluation of Gene Modification Strategies for Bloom Syndrome

Jumpstart2025Grant Assistance ProgramBloom Syndrome
Written By Million Dollar Bike Ride

Awardee: Caroline Kuo

Institution: University of California, Los Angeles

Awarded: $50,000

Funding Period: April 1, 2025 – March 31, 2026

Summary: To date, no studies have assessed the feasibility of gene modification as a potential treatment for Bloom syndrome. This project outlines specific aims that include proof-of-concept experiments essential for evaluating the viability of gene therapy as a therapeutic option for this condition

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